Drug for rare enzyme deficiency approved
Fri, 28 Apr 2006 05:57 PM EST
... The first-ever treatment for an extremely rare and often fatal genetic disease that interferes with the body’s ability to tap built-up stores of sugar for energy received federal approval. ...
Related Topics
- Rare Diseases
- Enzyme Therapy
- Trypsin
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- Lesch-Nyhan Syndrome
- Drug Safety
- Prescription Drugs
- Iron Deficiency Anemia
- Medium-chain acyl-coenzyme A dehydrogenase deficiency
- Mitochondrial trifunctional protein deficiency
- Vitamin B12 Deficiency
- G6PD
- Drug Side Effects
- Hereditary coproporphyria
- Drug Abuse
- Drug Information
- Exelon
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- Prescription Drug Abuse
- Prescription Drugs Abuse

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