Beta thalassemia |
Erythroblastic Anemia; thalassemia intermedia; Thalassemia Major |
Thalassemia (American English) (or thalassaemia in British English), also know as "Cooley's anemia", is an inherited disease of the red blood cells, classified as a hemoglobinopathy. The genetic defect results in synthesis of an abnormal hemoglobin molecule. The blood cells are vulnerable to mechanical injury and die easily. To survive, many people with thalassemia need blood transfusions at regular intervals. The disease's geographical association with the Mediterranean sea was responsible ...
Wikipedia - [full article]
Beta thalassemia Clinical Trials
- Combined Chelation Treatment with Deferiprone and Deferoxamine in Thalassemia Major
ClinicalTrials.gov Identifier: NCT00103753 - Active, not recruiting
beta-Thalassemia
- Genetic Factors Affecting the Severity of Beta Thalassemia
ClinicalTrials.gov Identifier: NCT00159042 - Recruiting
beta Thalassemia
- Extension Study on Efficacy and Safety of Deferasirox Treatment in Patients With Beta-Thalassemia and Transfusional Hemosiderosis
ClinicalTrials.gov Identifier: NCT00171301 - Active, not recruiting
Beta-Thalassemia Major
- Thalassemia Clinical Research Network - Cardiac L1/DFO Trial
ClinicalTrials.gov Identifier: NCT00115349 - Recruiting
Cardiovascular Diseases; Heart Diseases; Thalassemia; Anemia (Cooley''s); beta-Thalassemia
- Cardiac T2* in Beta-Thalassemia Patients on Deferasirox Treatment
ClinicalTrials.gov Identifier: NCT00447694 - Recruiting
Beta-Thalassemia; Iron Overload
- Evaluating the Safety of G-CSF Mobilization in Individuals With Beta Thalassemia Major
ClinicalTrials.gov Identifier: NCT00336362 - Recruiting
Beta-Thalassemia
- Safety & Efficacy of ICL670 vs. deferoxamine in Beta-thalassemia patients with iron overload due to blood transfusions
ClinicalTrials.gov Identifier: NCT00061750 - Completed
beta-Thalassemia
- Hydroxyurea to Treat Beta-Thalassemia (Cooley's Anemia)
ClinicalTrials.gov Identifier: NCT00001958 - Completed
Beta Thalassemia; Hemoglobinopathy
- 5-Azacytidine and Phenylbutyrate to Treat Severe Thalassemia
ClinicalTrials.gov Identifier: NCT00005934 - Completed
Beta Thalassemia
- Thalassemia (Cooley's Anemia) Clinical Research Network (TCRN)
ClinicalTrials.gov Identifier: NCT00000623 - Completed
Anemia (Cooley's); beta-Thalassemia; Blood Disease; Thalassemia; Osteoporosis
- Iron Balance Study of DFO and GT56-252 in Patients with Transfusional Iron Overload Secondary to Beta-Thalassemia
ClinicalTrials.gov Identifier: NCT00069862 - Completed
beta-Thalassemia
- A Study of Long-Term Treatment With Deferasirox in Patients With Beta-Thalassemia and Transfusional Hemosiderosis
ClinicalTrials.gov Identifier: NCT00171171 - Completed
Beta-Thalassemia; Hemosiderosis
- Study of ICL670 in iron overload from beta-thalassemia unable to be treated with deferoxamine or chronic anemias
ClinicalTrials.gov Identifier: NCT00061763 - Completed
beta-Thalassemia; Myelodysplastic Syndromes; Fanconi Syndrome; Anemia, Diamond-Blackfan; Anemia, Aplastic
- Evaluation of Subcutaneous Desferrioxamine as Treatment for Transfusional Hemochromatosis
ClinicalTrials.gov Identifier: NCT00000595 - Completed
Anemia (Iron-Loading); beta-Thalassemia; Hematologic Diseases; Hemoglobinopathies; Thalassemia; Iron Overload; Hemochromatosis
- Evaluating the Efficacy of Deferasirox in Transfusion Dependent Chronic Anaemias (Myelodysplastic Syndrome, Beta-Thalassaemia Patients) With Chronic Iron Overload
ClinicalTrials.gov Identifier: NCT00564941 - Not yet recruiting
Myelodysplastic Syndromes; Beta-Thalassemia
- Phase II Study of Arginine Butyrate With or Without Epoetin alfa in Patients With Thalassemia Intermedia
ClinicalTrials.gov Identifier: NCT00006136 - Completed
beta-Thalassemia
- Stem Cell Transplant in Sickle Cell Disease and Thalassemia
ClinicalTrials.gov Identifier: NCT00408447 - Recruiting
Sickle Cell Disease; Beta Thalassemia
- Chelation Therapy of Iron Overload With Pyridoxal Isonicotinoyl Hydrazone
ClinicalTrials.gov Identifier: NCT00000588 - Completed
Anemia (Iron-Loading); beta-Thalassemia; Hematologic Diseases; Hemoglobinopathies; Thalassemia; Iron Overload
- Stem Cell Transplantation after Reduced-Dose Chemotherapy for Patients with Sickle Cell Disease or Thalassemia
ClinicalTrials.gov Identifier: NCT00034528 - Active, not recruiting
Hemoglobinopathies; Anemia, Sickle Cell; Hemoglobin SC Disease; Thalassemia; Thalassemia Major
- Evaluating the Safety of Two Medications to Treat Hepatitis C in People With Thalassemia (The HepC Study)
ClinicalTrials.gov Identifier: NCT00502788 - Active, not recruiting
Hepatitis C; Thalassemia
- Genetics of Alpha Thalassemia in Israeli Ethnic Groups
ClinicalTrials.gov Identifier: NCT00159029 - Recruiting
alpha Thalassemia
- Detection of β Thalassemia Carriers by Red Cell Parameters Obtained From the H2 Automatic Counter
ClinicalTrials.gov Identifier: NCT00481221 - Recruiting
Thalassemia; Iron Deficiency
- Stem Cell Transplant in Patients With Thalassemia
ClinicalTrials.gov Identifier: NCT00578292 - Recruiting
Thalassemia
- Factors Promoting Increased Rate and Success of Pregnancy in the Thalassemia Population in Toronto
ClinicalTrials.gov Identifier: NCT00327639 - Recruiting
Thalassemia; Fertility; Pregnancy
- Zinc to Improve Bone Health in People With Thalassemia (The Think Zinc Study)
ClinicalTrials.gov Identifier: NCT00480415 - Recruiting
Thalassemia
- Zinc & Bone Health in Thalassemia: The Think Zinc Study
ClinicalTrials.gov Identifier: NCT00459732 - Recruiting
Thalassemia
- Endocrine and Nutritional Assessment in B Thalassemia Major
ClinicalTrials.gov Identifier: NCT00456690 - Not yet recruiting
Thalassemia
- An Extension Study of Iron Chelation Therapy With Deferasirox in β-Thalassemia Patients With Transfusional Iron Overload
ClinicalTrials.gov Identifier: NCT00171210 - Active, not recruiting
Transfusional Iron Overload in β-Thalassemia
- Iron Chelation Therapy With Deferasirox in β-Thalassemia Major Pediatric Patients With Transfusional Iron Overload
ClinicalTrials.gov Identifier: NCT00390858 - Active, not recruiting
Transfusional Iron Overload in β-Thalassemia Major
- Phase I Study to Examine the Effect of Deferasirox on Renal Hemodynamics in β-Thalassemia Patients With Transfusional Iron Overload
ClinicalTrials.gov Identifier: NCT00560820 - Recruiting
β-Thalassemia; Transfusional Iron Overload
- L-Glutamine Therapy for Sickle Cell Anemia and Sickle ß0 Thalassemia
ClinicalTrials.gov Identifier: NCT00125788 - Active, not recruiting
Sickle Cell Anemia (homozygous); Sickle ß0-Thalassemia
- Is IFN-Beta Treatment in MS Useful After a Washout Period in Patients With Neutralizing Antibodies to Interferon Beta
ClinicalTrials.gov Identifier: NCT00493116 - Active, not recruiting
Relapsing-Remitting Multiple Sclerosis
- Deferoxamine for the Treatment of Hemochromatosis
ClinicalTrials.gov Identifier: NCT00001203 - Active, not recruiting
Diabetes Mellitus; Heart Disease; Hemochromatosis; Thalassemia
- Study of Protein Translocation in Patients With Beta-Oxidation Disorders
ClinicalTrials.gov Identifier: NCT00004348 - Active, not recruiting
Beta-Oxidation Disorder; Peroxisomal Disorders
- Beta-Blocker Continuation Versus Interruption in Heart Failure Worsening
ClinicalTrials.gov Identifier: NCT00162565 - Recruiting
Heart Failure,Congestive; beta-Adrenergic Blockers
- Allogeneic Stem Cell Transplantation Following Chemotherapy in Patients with Hemoglobinopathies
ClinicalTrials.gov Identifier: NCT00153985 - Recruiting
Hemoglobinopathies; Sickle Cell Disease; Thalassemia
- Insulin Glargine (Lantus) vs Sulfonylurea (SU) for BETA Cell Function (BETA Study)
ClinicalTrials.gov Identifier: NCT00562172 - Recruiting
Type 2 Diabetes Mellitus
- Safety and antiviral study of ACH-126, 443 (beta-L-Fd4C) in the treatment of adults with HIV infection and modestly detectable viral load.
ClinicalTrials.gov Identifier: NCT00040157 - Active, not recruiting
HIV Infections
- Evaluation of Efficacy of Zoledronic Acid in Patients With Haemoglobin Syndromes (Thalassemia and Sicle Cell Anaemia) and Risk of Skeletal Events
ClinicalTrials.gov Identifier: NCT00346242 - Completed
Thalassemia
- Beta Alethine in Treating Patients With Low-Grade Lymphoma
ClinicalTrials.gov Identifier: NCT00007839 - Active, not recruiting
Lymphoma
- Safety Study of Interferon Beta 1a to for Acute Stroke
ClinicalTrials.gov Identifier: NCT00097318 - Active, not recruiting
Cerebrovascular Accident
- Study To Evaluate Beta Cell Function and Glycemic Outcome by Intensive Insulin Therapy
ClinicalTrials.gov Identifier: NCT00474838 - Recruiting
Type 2 Diabetes Mellitus; Pancreatic Beta Cell Function; Glucotoxicity
- Diagnostic Pilot Study of Dual Energy Absorptiometry in the Detection of Osteopenia or Osteoporosis in Patients With Thalassemia Major
ClinicalTrials.gov Identifier: NCT00006138 - Completed
Osteoporosis; Thalassemia Major; Osteopenia
- Beta Blockers Versus Variceal Band Ligation and Beta Blockers for Primary Prophylaxis of Variceal Bleeding
ClinicalTrials.gov Identifier: NCT00409084 - Recruiting
Esophageal Varices
- Randomized Trial of Beta-Carotene and Macular Degeneration
ClinicalTrials.gov Identifier: NCT00000152 - Active, not recruiting
Macular Degeneration
- L-glutamine Therapy for Sickle Cell Anemia
ClinicalTrials.gov Identifier: NCT00029887 - Recruiting
Anemia, Sickle Cell; Thalassemia
- Beta Alethine in Treating Patients With Waldenstrom's Macroglobulinemia
ClinicalTrials.gov Identifier: NCT00041379 - Active, not recruiting
Waldenstrom's Macroglobulinemia
- Monitoring of Erythroid Lineage Specific Chimerism Following Allogeneic Hematopoietic Transplantation for Thalassemia Major
ClinicalTrials.gov Identifier: NCT00480506 - Completed
Thalassemia Major
- Expanded Access of Deferasirox to Patients With Congenital Disorders of Red Blood Cells and Chronic Iron Overload
ClinicalTrials.gov Identifier: NCT00235391 - Active, not recruiting
Thalassemia; Sickle Cell Disease; Diamond Blackfan Anemia; Myelofibrosis
- Phase I/II Study of Nonmyeloablative Allogeneic Bone Marrow Transplantation in Patients With High Risk Hemoglobinopathy
ClinicalTrials.gov Identifier: NCT00005897 - Recruiting
Graft Versus Host Disease; Sickle Cell Anemia; Thalassemia
- Clinical and Laboratory Assessment of Iron Overload in Sickle Cell Anemia and Sickle Cell Thalassemia
ClinicalTrials.gov Identifier: NCT00512564 - Not yet recruiting
Sickle Cell Anemia; Sickle Cell Thalassemia
- Safety and antiviral study of ACH-126, 443 (beta-L-Fd4C) in the treatment of adults with chronic Hepatitis B infection.
ClinicalTrials.gov Identifier: NCT00037622 - Active, not recruiting
Chronic Hepatitis B
- Piperacillin/Tazobactam for Bacteremia With Organisms Producing Chromosomally-Encoded AmpC Beta-Lactamase
ClinicalTrials.gov Identifier: NCT00414193 - Recruiting
Bacteremia; AmpC Beta-Lactamase
- Efficacy Study in Removing Excess Iron from the Heart
ClinicalTrials.gov Identifier: NCT00105495 - Completed
Thalassemia Major; Hemosiderosis
- Hu-Mik-(Beta)1 to Treat T-Cell Large Granular Lymphocytic Leukemia
ClinicalTrials.gov Identifier: NCT00076180 - Recruiting
Leukemia, T-Cell
- beta-Glucan and Monoclonal Antibody in Treating Patients With Metastatic Neuroblastoma
ClinicalTrials.gov Identifier: NCT00037011 - Active, not recruiting
disseminated neuroblastoma; recurrent neuroblastoma
- Safety and Tolerability of Interferon-Beta-1a and Estroprogestins Association in MS Patients
ClinicalTrials.gov Identifier: NCT00151801 - Recruiting
Multiple Sclerosis
- A Pilot Study of HSCT for Patients With High-Risk Hemoglobinopathy Using a Nonmyeloablative Preparative Regimen
ClinicalTrials.gov Identifier: NCT00427661 - Recruiting
Sickle Cell Disease; Thalassemia; Hemoglobinopathies
- Stem Cell Transplant for Hemoglobinopathy
ClinicalTrials.gov Identifier: NCT00176852 - Recruiting
Sickle Cell Disease; Thalassemia
- Long-Acting Beta Agonist Response by Genotype
ClinicalTrials.gov Identifier: NCT00200967 - Active, not recruiting
Asthma
- Effects of (1,3), (1,6)-Beta-D-Glucan on Insulin Sensitivity and Inflammatory Markers of the Metabolic Syndrome
ClinicalTrials.gov Identifier: NCT00403689 - Active, not recruiting
Overweight
- A Study of NeoRecormon (Epoetin Beta) in Patients With End Stage Renal Disease.
ClinicalTrials.gov Identifier: NCT00413101 - Active, not recruiting
Anemia
- Elder Surgery - Functional Recovery Following Beta Blockade
ClinicalTrials.gov Identifier: NCT00507663 - Active, not recruiting
Post Operative Cognitive Dysfunction
- Beta-Carotene and Alpha-Tocopherol Chemoprevention of Second Primary Malignancies in Head and Neck Cancer Patients
ClinicalTrials.gov Identifier: NCT00169845 - Active, not recruiting
Neoplasms
- Investigating if Interferon-Beta Can be Used in Patients With MS After They Have Developed Neutralizing Antibodies
ClinicalTrials.gov Identifier: NCT00492466 - Active, not recruiting
Relapsing-Remitting Multiple Sclerosis
- Interferon-beta Treatment of Ulcerative Colitis
ClinicalTrials.gov Identifier: NCT00048347 - Recruiting
Ulcerative Colitis
- Iron Overload Assesment in Sickle Cell Anemia and Sickle Cell Thalassemia
ClinicalTrials.gov Identifier: NCT00512226 - Not yet recruiting
Sickle Cell Anemia; Sickle Cell Thalassemia; Iron Overload; MRI
- Beta Alethine in Treating Patients With Myeloma
ClinicalTrials.gov Identifier: NCT00006466 - Active, not recruiting
monoclonal gammopathy of undetermined significance; stage I multiple myeloma; stage II multiple myeloma; extramedullary plasmacytoma; ...
- Surveillance of Streptococcal Infections in Children in India
ClinicalTrials.gov Identifier: NCT00342199 - Active, not recruiting
Group A Beta Hemolytic Streptococcal (GAS) Infection
- Extension Study of Iron Chelation Therapy With Deferasirox in β-Thalassemia and Other Patients With Rare Chronic Anemia and Transfusional Iron Overload
ClinicalTrials.gov Identifier: NCT00303329 - Active, not recruiting
Transfusional Iron Overload in Patients With Chronic Anemia
- The Effect of Beta-Blockers and Aspirin on Hemostasis and Endothelial Function After Acute Mental Stress
ClinicalTrials.gov Identifier: NCT00174902 - Active, not recruiting
Arteriosclerosis; Stress, Psychological
- Treatment of Menstrual Migraine With Sequential, Transdermal, 17-Beta-Estradiol. A Double-Blind, Randomised, Cross-Over Trial.
ClinicalTrials.gov Identifier: NCT00204074 - Active, not recruiting
Migraine
- Pilot Study on Safety and Efficacy of MD05 in Comparison With Beta-TCP in Patients Undergoing Sinus Floor Augmentation
ClinicalTrials.gov Identifier: NCT00520377 - Active, not recruiting
Alveolar Ridge Augmentation
- Luteal Phase FSH in the IVF Poor Reponder
ClinicalTrials.gov Identifier: NCT00225433 - Active, not recruiting
Infertility
- A Study of Beta-Lactam in Hospitalized Patients With Skin and Skin Structure Infections
ClinicalTrials.gov Identifier: NCT00303589 - Active, not recruiting
Soft Tissue Infections
- Treatment of Congenital Stationary Night Blindness With an Alga Containing High Dose of Beta Carotene
ClinicalTrials.gov Identifier: NCT00569023 - Enrolling by invitation
Night Blindness
- Alpha-Tocopherol, Beta-Carotene Cancer Prevention (ATBC) Study
ClinicalTrials.gov Identifier: NCT00342992 - Active, not recruiting
Lung Cancer; Prostatic Neoplasms; Prostate Cancer; Pancreatic Cancer
- A Study of NeoRecormon (Epoetin Beta), CellCept (Mycophenolate Mofetil) and Prednisone in Patients With Low or Intermediate Myelodysplastic Syndromes.
ClinicalTrials.gov Identifier: NCT00551291 - Active, not recruiting
Myelodysplastic Syndromes
- Beta Blockade in Critical Injury
ClinicalTrials.gov Identifier: NCT00356187 - Recruiting
Trauma
- Beta-Blocker Before Extubation
ClinicalTrials.gov Identifier: NCT00563238 - Recruiting
Myocardial Ischemia
- Beta-Glucan and Rituximab in Treating Young Patients With Relapsed or Progressive Lymphoma or Leukemia, or Lymphoproliferative Disorder Related to Donor Stem Cell Transplantation
ClinicalTrials.gov Identifier: NCT00087009 - Recruiting
childhood Hodgkin's lymphoma; childhood non-Hodgkin's lymphoma; Leukemia; Lymphoma
- Beta-2 Polymorphisms and Beta Receptor Selectivity
ClinicalTrials.gov Identifier: NCT00214318 - Completed
Heart Failure
- Beta Blocker for Chronic Wound Healing
ClinicalTrials.gov Identifier: NCT00368602 - Recruiting
Ulcer; Burns
- Beta Cell Function in Women With Turner Syndrome
ClinicalTrials.gov Identifier: NCT00419107 - Active, not recruiting
Turner Syndrome
- Beta-Cell Function and Sitagliptin Trial (BEST)
ClinicalTrials.gov Identifier: NCT00420511 - Recruiting
Type 2 Diabetes Mellitus
- Evaluation of [123I] MNI-308 and SPECT as a Marker of Beta-Amyloid Protein Deposition in Subjects With Alzheimer Disease in Comparison to Healthy Subjects
ClinicalTrials.gov Identifier: NCT00544453 - Active, not recruiting
Alzheimer Disease
- Avonex (Interferon-Beta-1a) and Avonex Plus Methylprednisolone for the Treatment of Relapsing-Remitting MS
ClinicalTrials.gov Identifier: NCT00168766 - Active, not recruiting
Relapsing-Remitting Multiple Sclerosis
- Gene Expression in MS Patients Before and During Treatment With Interferon-Beta
ClinicalTrials.gov Identifier: NCT00202384 - Recruiting
Multiple Sclerosis
- BOAT: Beta Blocker Uptitration With OptiVol After CRT.
ClinicalTrials.gov Identifier: NCT00433043 - Recruiting
Congestive Heart Failure
- Treatment of the Anemia of Myelodysplastic Syndromes by the Association of Epoetin Beta and All Trans Retinoic Acid
ClinicalTrials.gov Identifier: NCT00437450 - Active, not recruiting
Anemia in Myelodysplastic Syndromes
- Physicians' Health Study II: Vitamin E, Ascorbic Acid, Beta Carotene, and/or Multivitamins in Preventing Cancer and Cardiovascular Disease in Older Healthy Male Doctors
ClinicalTrials.gov Identifier: NCT00270647 - Active, not recruiting
Colorectal Cancer; Prostate Cancer; Unspecified Adult Solid Tumor, Protocol Specific
- BEYOND Study - Betaferon/Betaseron Efficacy Yielding Outcomes of a New Dose in Multiple Sclerosis (MS) Patients
ClinicalTrials.gov Identifier: NCT00099502 - Active, not recruiting
Multiple Sclerosis
- Preservation of Pancreatic Beta Cell Function Through Insulin Pump Therapy
ClinicalTrials.gov Identifier: NCT00574405 - Recruiting
Diabetes Mellitus
- Collaborative Initial Glaucoma Treatment Study (CIGTS)
ClinicalTrials.gov Identifier: NCT00000149 - Active, not recruiting
Open-Angle Glaucoma
- Effect of AC2993 with or without Immunosuppression on Beta Cell Function in Patients with Type I Diabetes
ClinicalTrials.gov Identifier: NCT00064714 - Active, not recruiting
Diabetes Mellitus
- Rebif® New Formulation in Relapsing Forms of Multiple Sclerosis (RMS)
ClinicalTrials.gov Identifier: NCT00110396 - Active, not recruiting
Multiple Sclerosis
- Combination Therapy with Avonex and BiMonthly High Dose Intravenous Methotrexate in Multiple Sclerosis
ClinicalTrials.gov Identifier: NCT00037102 - Active, not recruiting
Multiple Sclerosis
- Minocycline as Add-on to Interferon-Beta-1a (Rebif®) in RRMS (Recycline)
ClinicalTrials.gov Identifier: NCT00381459 - Recruiting
Relapsing-Remitting Multiple Sclerosis
- Epidemiology of Community - Associated Extended-Spectrum Beta-Lactamases (ESBL) Producing Escherichia Coli
ClinicalTrials.gov Identifier: NCT00573235 - Recruiting
Enterobacteriaceae Infections
- Preservation of Beta-Cell Function in Type 2 Diabetes Mellitus
ClinicalTrials.gov Identifier: NCT00232583 - Active, not recruiting
Type 2 Diabetes Mellitus

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